The MDA Engage seminar in Hershey, Pennsylvania, brought together neuromuscular families and specialists for education and ...

Able,” a short film starring my girlfriend, Amanda, and me, was selected for inclusion in AN/OTHER Film Festival in Fremantle ...

The FDA is considering whether to conditionally approve a new treatment for DMD patients with mutations amenable to exon 51 ...

Commendamide, a metabolite produced by beneficial gut bacteria that are depleted in people with DMD, protects muscle cells ...

CureDuchenne has launched a national public service announcement campaign to highlight the urgent need for new treatments for ...

After two difficult years, columnist Betty's Vertin's son Max won't go back to college this fall, a decision that has her breathing easier.

There are 24 hours in a day, so there should be enough time in each one to keep from feeling caregiver burnout, says columnist.

People with Duchenne muscular dystrophy (DMD) require some level of caregiving throughout their whole lives, particularly as the disease progresses and patients become less mobile and more reliant on ...

Muscular dystrophy (MD) refers to a group of inherited muscle disorders caused by mutations in genes that generate proteins that play an essential role in muscle structure and function. The disease ...

During a recent facioscapulohumeral muscular dystrophy (FSHD) wellness group meeting via Zoom, a friend of mine shared a poem by May Sarton that prompted the question: “Do I think of my body as an old ...

While Duchenne muscular dystrophy (DMD) is one of the most common types of this group of muscle-wasting disorders, affecting about 1 in 3,500 male births, each patient’s journey with this form of ...

Exon skipping is a treatment approach for people whose Duchenne muscular dystrophy is due to certain mutations in its causative gene. Exon skipping works like a molecular patch, so that the DMD gene ...