Upsher-Smith Laboratories launched DMD treatment Kymbee in the U.S., backed by a support program for patients.

Columnist Shalom Lim attended a musical honoring healthcare professionals and, as someone with Duchenne MD, came away feeling ...

A regimen of three immune-suppressing drugs may improve the effectiveness of gene therapy for people with DMD, research in ...

Columnist Robin Stemple struggles to feel grateful on difficult days with FSHD, but still tries to recognize his many ...

The holiday season is upon us, and I am already exhausted. I’m well aware of everything I need to do in December, so being this tired already isn’t great. It makes me think about the opening lines of ...

Columnist Betty Vertin's track career ended years ago, but she never stopped lifting weights — only now its the emotional weight of Duchenne.

A Phase 1/2 clinical trial testing SRP-1003 for myotonic dystrophy type 1 is progressing with higher doses as planned.

New research shows DMD is marked by abnormalities in muscle development in the womb, supporting the potential of a therapy ...

When in the course of human events, it becomes necessary to make choices, we must first consider our options. Congratulations! By reading these words, you have made a choice to crawl into my brain ...

Agamree (vamorolone), a type of corticosteroid approved to help preserve muscle function in people with Duchenne muscular dystrophy (DMD), appears to work as well as traditional corticosteroids at ...

The U.S. Food and Drug Administration (FDA) has approved an update to the prescribing information for Duchenne muscular dystrophy (DMD) gene therapy Elevidys (delandistrogene moxeparvovec-rokl), ...