After teasing a new regulatory process for personalized genetic medicines at the end of last year, the FDA today unveiled draft guidance for an approval pathway that could see custom CRISPR therapies, ...

Jason Mast is a general assignment reporter at STAT focused on the science behind new medicines and the systems and people that decide whether that science ever reaches patients. You can reach Jason ...

The parasympathetic nervous system (PNS), a division of the autonomic nervous system (ANS), is responsible for regulating bodily functions during rest. Unlike its counterpart, the sympathetic nervous ...

The Plausible Mechanism Pathway allows FDA drug approval without randomized trials, focusing on diseases with known biological causes. This pathway targets rare genetic diseases, emphasizing biologic ...

The plausible mechanism pathway “could accelerate gene therapy/editing development,” analysts at William Blair said Thursday, while adding that additional clarity is needed. Individualized therapies ...

NEW YORK, Nov 12 (Reuters) - The U.S. Food and Drug Administration can approve new personalized treatments for rare and deadly genetic diseases based on data from a handful of patients, two of the ...

Elaine Chen covers biotech, co-writes The Readout newsletter, and co-hosts STAT’s weekly biotech podcast, The Readout Loud. You can reach Elaine on Signal at elaineywchen.70. Compass Pathways, which ...

In recent years, hundreds of community colleges have embraced the guided pathways model, a sweeping set of large-scale reforms to better steer students through academic programs and boost completion ...

BYU-Pathway Worldwide students in Lagos, Nigeria gather in March 2024. Enrollment in Nigeria surged from 6,603 students in 2023 to 11,724 in 2024. With higher education experiencing unprecedented ...

Doximity has acquired the AI startup Pathway Medical for $63 million. Pathway has one of the largest structured datasets in medicine, Doximity said. The integration is underway, and the companies are ...

To more fully explore the perspectives and motivations of those two groups, we partnered with the New York-based social-science research firm Langer Research Associates. The resulting project ...

The alternative complement pathway plays a key role in the pathogenesis of IgA nephropathy. Iptacopan specifically binds to factor B and inhibits the alternative pathway. In this phase 3, double-blind ...