The MDA Engage seminar in Hershey, Pennsylvania, brought together neuromuscular families and specialists for education and ...

Able,” a short film starring my girlfriend, Amanda, and me, was selected for inclusion in AN/OTHER Film Festival in Fremantle ...

The FDA is considering whether to conditionally approve a new treatment for DMD patients with mutations amenable to exon 51 ...

Columnist Betty Vertin shares big news about a bigger house her family is buying that will better accommodate her sons with Duchenne MD.

CureDuchenne has launched a national public service announcement campaign to highlight the urgent need for new treatments for ...

Commendamide, a metabolite produced by beneficial gut bacteria that are depleted in people with DMD, protects muscle cells ...

After two difficult years, columnist Betty's Vertin's son Max won't go back to college this fall, a decision that has her breathing easier.

We are pleased to partner with the Muscular Dystrophy Association (MDA) to bring you coverage from the MDA Engage Symposium.

Muscular dystrophy (MD) refers to a group of inherited muscle disorders caused by mutations in genes that generate proteins that play an essential role in muscle structure and function. The disease ...

Exon skipping is a treatment approach for people whose Duchenne muscular dystrophy is due to certain mutations in its causative gene. Exon skipping works like a molecular patch, so that the DMD gene ...

While Duchenne muscular dystrophy (DMD) is one of the most common types of this group of muscle-wasting disorders, affecting about 1 in 3,500 male births, each patient’s journey with this form of ...

Going to school for the first time is an important moment in a child’s life. The educational journey for a child with Duchenne muscular dystrophy (DMD) can be exciting but also challenging. To smooth ...